Letters to the Editor
Vol. 4 No. 3 (2025)
Gene therapy for hemophilia B
Publisher's note
All claims expressed in this article are solely those of the authors and do not necessarily represent those of their affiliated organizations, or those of the publisher, the editors and the reviewers. Any product that may be evaluated in this article or claim that may be made by its manufacturer is not guaranteed or endorsed by the publisher.
All claims expressed in this article are solely those of the authors and do not necessarily represent those of their affiliated organizations, or those of the publisher, the editors and the reviewers. Any product that may be evaluated in this article or claim that may be made by its manufacturer is not guaranteed or endorsed by the publisher.
Published: 12 December 2025
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To report that the first gene therapy procedure in Italy for the treatment of severe or moderately severe hemophilia B has been successfully administered at the Policlinico of Milan, Italy
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Citations
1. Castaman G. Gene transfer in hemophilia B: a big stepforward. Bleeding Thromb Vasc Biol 2023;2:70. DOI: https://doi.org/10.4081/btvb.2023.70
2. Di Minno G, Spadarella G, Calcaterra IL, et al. The evolving landscape of gene therapy for congenital severe hemophilia: a 2024 state of the art. Bleeding Thromb Vasc Biol 2024;3:144. DOI: https://doi.org/10.4081/btvb.2024.144
3. Mannucci PM. Gene transfer in hemophilia A: not cogent yet. Bleeding Thromb Vasc Biol 2022;1:32. DOI: https://doi.org/10.4081/btvb.2022.32
4. Mannucci PM. Growing weapons to fight hemophilia. Bleeding Thromb Vasc Biol 2023;2:64. DOI: https://doi.org/10.4081/btvb.2023.64
How to Cite
1.
Mannucci PM. Gene therapy for hemophilia B. Bleeding Thromb Vasc Biol [Internet]. 2025 Dec. 12 [cited 2026 Mar. 28];4(3). Available from: https://www.btvb.org/btvb/article/view/425
Copyright (c) 2025 The Author(s)
This work is licensed under a Creative Commons Attribution-NonCommercial 4.0 International License.
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