Letters to the Editor
Vol. 4 No. 3 (2025)
Gene therapy for hemophilia B
Publisher's note
All claims expressed in this article are solely those of the authors and do not necessarily represent those of their affiliated organizations, or those of the publisher, the editors and the reviewers. Any product that may be evaluated in this article or claim that may be made by its manufacturer is not guaranteed or endorsed by the publisher.
All claims expressed in this article are solely those of the authors and do not necessarily represent those of their affiliated organizations, or those of the publisher, the editors and the reviewers. Any product that may be evaluated in this article or claim that may be made by its manufacturer is not guaranteed or endorsed by the publisher.
Published: 12 December 2025
258
Views
10
Downloads
Authors
Dear Editor,
I wish to report that the first gene therapy procedure in Italy for the treatment of severe or moderately severe hemophilia B has been successfully administered at the Policlinico of Milan....
Downloads
Download data is not yet available.
Citations
1. Castaman G. Gene transfer in hemophilia B: a big stepforward. Bleeding Thromb Vasc Biol 2023;2:70. DOI: https://doi.org/10.4081/btvb.2023.70
2. Di Minno G, Spadarella G, Calcaterra IL, et al. The evolving landscape of gene therapy for congenital severe hemophilia: a 2024 state of the art. Bleeding Thromb Vasc Biol 2024;3:144. DOI: https://doi.org/10.4081/btvb.2024.144
3. Mannucci PM. Gene transfer in hemophilia A: not cogent yet. Bleeding Thromb Vasc Biol 2022;1:32. DOI: https://doi.org/10.4081/btvb.2022.32
4. Mannucci PM. Growing weapons to fight hemophilia. Bleeding Thromb Vasc Biol 2023;2:64. DOI: https://doi.org/10.4081/btvb.2023.64
How to Cite
1.
Mannucci PM. Gene therapy for hemophilia B. Bleeding Thromb Vascul Biol [Internet]. 2025 Dec. 12 [cited 2026 Jan. 6];4(3). Available from: https://www.btvb.org/btvb/article/view/425
Copyright (c) 2025 The Author(s)
This work is licensed under a Creative Commons Attribution-NonCommercial 4.0 International License.
Similar Articles
- CO38 | Management of pregnancy, delivery, and postpartum in Italian carriers and women with hemophilia A and B , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- CO33 | Acquired hemophilia A in Liguria, Italy: what six years of data reveal , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- PO02 | Pregnancy and delivery in women with hemophilia and carriers are still challenging: a ten years analysis from The Italian Association of Hemophilia Centers (AICE) , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- PO49 | Use of emicizumab in two patients with acquired hemophilia A: a new therapeutic approach , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- CO51 | Novel biomarkers of neurological damage in acute immune-mediated thrombotic thrombocytopenic purpura , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- PO39 | Bleeding events in Von Willebrand disease type 1 yearly treatable with desmopressin , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- PO12 | Characterisation and real word clinical data of HEM006, a newly formulated intranasal spray desmopressin (DDAVP) to address a global treatment gap , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- Daniela Poli, Riccardo Tartaglia, Doris Barcellona , Paolo Bucciarelli , Antonio Ciampa, Elvira Grandone, Giuseppe Malcangi, Giuseppe Rescigno, Vincenzo Toschi, Sophie Testa, Alessandro Squizzato, Attitude to clinical research among health professionals affiliated with the Italian Federation of Centers for the Diagnosis of Thrombotic Disorders and the Surveillance of the Antithrombotic Therapies (FCSA) , Bleeding, Thrombosis and Vascular Biology: Vol. 2 No. 1 (2023)
- CO49 | The burden of cerebral small vessel disease in ITTP patients from acute phase to remission , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
- CO31 | Immune system profiling in FVIII-treated and emicizumab-treated pediatric HA patients , Bleeding, Thrombosis and Vascular Biology: Vol. 4 No. s1 (2025)
You may also start an advanced similarity search for this article.
Most read articles by the same author(s)
- Pier Mannuccio Mannucci, Gene transfer in hemophilia A: not cogent yet , Bleeding, Thrombosis and Vascular Biology: Vol. 1 No. 1 (2022)
- Pier Mannuccio Mannucci, An ecological alliance against air pollution and cardiovascular disease , Bleeding, Thrombosis and Vascular Biology: Vol. 1 No. 1 (2022)
- Pier Mannuccio Mannucci, Growing weapons to fight hemophilia , Bleeding, Thrombosis and Vascular Biology: Vol. 2 No. 1 (2023)
